Sarepta Announces Clinical Hold Lifted for its Duchenne Muscular Dystrophy Micro-dystrophin Gene Therapy Program
09/24/18 7:00 AM EDT
“Thanks to the diligent and rapid work of my Sarepta colleagues and Nationwide Children’s Hospital in compiling and submitting a complete response and the expeditious evaluation by the
This press release contains "forward-looking statements." Any statements contained in this press release that are not statements of historical fact may be deemed to be forward-looking statements. Words such as "believes," "anticipates," "plans," "expects," "will," "intends," "potential," "possible" and similar expressions are intended to identify forward-looking statements. These forward-looking statements include statements regarding Sarepta’s focus on meeting with the Division to take guidance and gain alignment around what Sarepta hopes to be its registration trial for its micro-dystrophin program; Sarepta’s expectation that the DMD micro-dystrophin gene therapy program will not be delayed due to the clinical hold; and Sarepta’s goal to commence the DMD micro-dystrophin gene therapy by year-end 2018.
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Source: Sarepta Therapeutics, Inc.
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